SMA valiant trial: A prospective, double-blind, placebo-controlled trial of valproic acid in ambulatory adults with spinal muscular atrophy

John T. Kissel, Bakri Elsheikh, Wendy M. King, Miriam Freimer, Charles B. Scott, Stephen J. Kolb, Sandra P. Reyna, Thomas O. Crawford, Louise R. Simard, Kristin J. Krosschell, Gyula Acsadi, Mary K. Schroth, Guy D'Anjou, Bernard Lasalle, Thomas W. Prior, Susan Sorenson, Jo Anne Maczulski, Kathryn J. Swoboda

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45 Scopus citations

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Nursing and Health Professions

Medicine and Dentistry

Pharmacology, Toxicology and Pharmaceutical Science