Rare Disease Innovation at the FDA - Opportunities for Implementation

Carolyn K. Shore, Tequam L. Worku, Jeffrey Kahn

Research output: Contribution to journalShort surveypeer-review

Original languageEnglish (US)
JournalJAMA
Volume332
Issue number23
DOIs
StatePublished - Dec 17 2024
Externally publishedYes

ASJC Scopus subject areas

  • General Medicine

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