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Neuronal SMN expression corrects spinal muscular atrophy in severe SMA mice while muscle-specific SMN expression has no phenotypic effect

  • Tatiana O. Gavrilina
  • , Vicki L. McGovern
  • , Eileen Workman
  • , Thomas O. Crawford
  • , Rocky G. Gogliotti
  • , Christine J. Didonato
  • , Umrao R. Monani
  • , Glenn E. Morris
  • , Arthur H.M. Burghes

Research output: Contribution to journalArticlepeer-review

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Biochemistry, Genetics and Molecular Biology

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