Neuronal SMN expression corrects spinal muscular atrophy in severe SMA mice while muscle-specific SMN expression has no phenotypic effect
- Tatiana O. Gavrilina
- , Vicki L. McGovern
- , Eileen Workman
- , Thomas O. Crawford
- , Rocky G. Gogliotti
- , Christine J. Didonato
- , Umrao R. Monani
- , Glenn E. Morris
- , Arthur H.M. Burghes
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