Highly efficient biallelic correction of homozygous COL7A1 mutation using ABE8e adenine base editor

Imogen R. Brooks, Yara Alrokh, Aidin Kazemizadeh, Katarzyna Balon, Gregory Newby, David R. Liu, Łukasz Łaczmański, John A. McGrath, Joanna Jacków-Malinowska

Research output: Contribution to journalLetterpeer-review

Original languageEnglish (US)
Pages (from-to)583-585
Number of pages3
JournalBritish Journal of Dermatology
Volume190
Issue number4
DOIs
StatePublished - Apr 2024
Externally publishedYes

ASJC Scopus subject areas

  • Dermatology

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