Genetic Modification of Huntington Disease Acts Early in the Prediagnosis Phase

Jeffrey D. Long, Jong Min Lee, Elizabeth H. Aylward, Tammy Gillis, Jayalakshmi Srinidhi Mysore, Kawther Abu Elneel, Michael J. Chao, Jane S. Paulsen, Marcy E. MacDonald, James F. Gusella

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Medicine & Life Sciences