Expanded Access for Nusinersen in Patients With Spinal Muscular Atropy: Negotiating Limited Data, Limited Alternative Treatments, and Limited Hospital Resources

Benjamin S. Wilfond, Christian Morales, Holly A. Taylor

Research output: Contribution to journalArticlepeer-review

1 Scopus citations
Original languageEnglish (US)
Pages (from-to)66-67
Number of pages2
JournalAmerican Journal of Bioethics
Volume17
Issue number10
DOIs
StatePublished - Oct 3 2017

ASJC Scopus subject areas

  • Issues, ethics and legal aspects
  • Health Policy

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