@article{fe0b08cbe93c4989ba842c8f33160aa8,
title = "A decade of optimizing drug development for rare neuromuscular disorders through TACT",
abstract = "This year marks the tenth anniversary of the TREAT-NMD Advisory Committee for Therapeutics (TACT), a group of multidisciplinary experts that evaluates drug development programmes for rare neuromuscular diseases and identifies pitfalls. Here, we discuss the experience with TACT based on its reviews of more than 50 applications and its potential as a model for other rare disorders.",
author = "Wagner, {Kathryn R.} and {De Luca}, Annamaria and Didier Caizergues and James Dowling and Nathalie Goemans and Heather Gordish-Dressman and Grounds, {Miranda D.} and Michael Kelly and Anna Mayhew and McNally, {Elizabeth M.} and Tracey Zoetis and Joanne Lee and Cathy Turner and Wells, {Dominic J.} and Cristina Csimma and Volker Straub",
note = "Publisher Copyright: {\textcopyright} 2020, Nature.",
year = "2020",
month = jan,
day = "1",
doi = "10.1038/d41573-019-00199-1",
language = "English (US)",
volume = "19",
journal = "Nature Reviews Drug Discovery",
issn = "1474-1776",
publisher = "Nature Research",
number = "1",
}